CMT Treatment Report

www.CMTTreatmentReport.com

Phase 2

Phase I/IIa Trial of scAAV1.tMCK.NTF3 for Treatment of Charcot-Marie-Tooth Type 1A (CMT1A)

https://clinicaltrials.gov/ct2/show/NCT03520751?type=Intr&cond=Charcot-Marie-Tooth&lupd_s=11%2F21%2F2018&lupd_d=14

Phase I/IIa Trial of scAAV1.tMCK.NTF3 for Treatment of CMT1A

Condition :   Charcot-Marie-Tooth Neuropathy Type 1A

Intervention :   Drug: scAAV1.tMCK.NTF3

Sponsor :   Nationwide Children’s Hospital

Recruiting

NCT03520751

Thu, 10 May 2018 12:00:00 EDT

Dec 5, 2018 update – start date delayed +3 months from oct 2018 to jan 2019
Feb 20, 2019 update – start date delayed again +6 months from jan 2019 to july 2019
Jun 13, 2019 update – status changed from recruiting to not yet recruiting [is this normal? was it recruiting before? find out] Oct 16, 2019 update – start date delayed again +6 months from jul 2019 to jan 2020
Nov 19, 2020 update – recruiting

Extension Study to Evaluate the Long-Term Effects of ACE-083 in Patients With Charcot-Marie Tooth (CMT) Disease Type 1 (CMT1) and Type X (CMTX) [Terminated]

https://clinicaltrials.gov/ct2/show/NCT03943290?type=Intr&cond=Charcot-Marie-Tooth&lupd_s=04%2F25%2F2019&lupd_d=14

Extension Study to Evaluate the Long-Term Effects of ACE-083 in Patients With Facioscapulohumeral Muscular Dystrophy (FSHD) and Charcot-Marie Tooth (CMT) Disease Types 1 and X (CMT1 and CMTX)

Conditions :   Facioscapulohumeral Muscular Dystrophy;   Charcot-Marie-Tooth Disease

Intervention :   Drug: ACE-083

Sponsor :   Acceleron Pharma, Inc.

Recruiting

NCT03943290

Thu, 09 May 2019 12:00:00 EDT

Study of ACE-083 in Patients With Charcot-Marie-Tooth Disease

https://clinicaltrials.gov/ct2/show/NCT03124459?type=Intr&cond=Charcot-Marie-Tooth&lupd_s=10%2F30%2F2018&lupd_d=14

Study of ACE-083 in Patients With Charcot-Marie-Tooth Disease

Condition :   Charcot-Marie-Tooth Disease

Interventions :   Drug: ACE-083;   Drug: Placebo

Sponsor :   Acceleron Pharma, Inc.

Recruiting

NCT03124459

Fri, 21 Apr 2017 12:00:00 EDT

  • added more locations
  • dec 5, 2018 updated
  • jan 15, 2019 updated (vermont study location added)
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